OPA1 GENE MUTATION
Clinical trials for OPA1 GENE MUTATION explained in plain language.
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New eye drug hopes to slow inherited blindness
Disease control Recruiting nowThis early-stage study tests a new medicine called PYC-001, given as an injection into the eye, for people with a rare genetic eye disease (autosomal dominant optic atrophy) caused by a change in the OPA1 gene. The main goal is to check the safety of different doses and schedules…
Matched conditions: OPA1 GENE MUTATION
Phase: PHASE1, PHASE2 • Sponsor: PYC Therapeutics • Aim: Disease control
Last updated Jul 01, 2026 00:00 UTC
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Can eye tests track an inherited form of blindness?
Knowledge-focused Recruiting nowThis study follows people with a genetic condition called OPA1-associated optic atrophy, which causes gradual vision loss. Researchers will use a battery of eye exams—including vision charts, contrast sensitivity, and retinal imaging—to see how the disease changes over time. The …
Matched conditions: OPA1 GENE MUTATION
Sponsor: Ludwig-Maximilians - University of Munich • Aim: Knowledge-focused
Last updated Jul 30, 2026 00:00 UTC