OPA1 GENE MUTATION

Clinical trials for OPA1 GENE MUTATION explained in plain language.

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Trials to join now! 1 Not yet finished but already full! 1

First human trial for genetic eye disease treatment begins

Disease control Recruiting now

This early-stage study is testing the safety of a new eye injection called PYC-001 in adults with a specific genetic condition that causes progressive vision loss (OPA1-related optic atrophy). About 21 participants in the UK and Australia will receive different doses and schedule…

Matched conditions: OPA1 GENE MUTATION

Phase: PHASE1, PHASE2 • Sponsor: PYC Therapeutics • Aim: Disease control

Last updated Mar 30, 2026 14:32 UTC

OPA1 GENE MUTATION

Get alerted when new OPA1 GENE MUTATION trials appear

First human trial for genetic eye disease treatment begins