New eye drug hopes to slow inherited blindness
NCT ID NCT06970106
First seen Nov 01, 2025 · Last updated Jun 15, 2026 · Updated 33 times
Summary
This early-stage study tests a new medicine called PYC-001, given as an injection into the eye, for people with a rare genetic eye disease (autosomal dominant optic atrophy) caused by a change in the OPA1 gene. The main goal is to check the safety of different doses and schedules in about 18 adults from Australia, New Zealand, and other APAC countries. Researchers will also look at whether the treatment can help preserve or improve vision.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Cerulea Clinical Trials
RECRUITINGEast Melbourne, Australia
Contact
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Retina Specialists
RECRUITINGAuckland, 1052, New Zealand
Contact
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Save Sight Institute - Sydney Eye Hospital
RECRUITINGSydney, New South Wales, 2000, Australia
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact
Conditions
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