HYPOCHONDROPLASIA
Clinical trials for HYPOCHONDROPLASIA explained in plain language.
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Hope for kids with rare bone disorder: new drug shows promise in Long-Term trial
Disease control ENROLLING_BY_INVITATIONThis study is for children with hypochondroplasia, a condition that causes short stature and bone differences. Researchers are testing a drug called infigratinib to see if it is safe and helps improve growth over the long term. Participants must have already completed a previous …
Matched conditions: HYPOCHONDROPLASIA
Phase: PHASE2 • Sponsor: QED Therapeutics, a BridgeBio company • Aim: Disease control
Last updated Jun 27, 2026 12:37 UTC
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New drug aims to help short-statured children grow taller
Disease control OngoingThis study tests a drug called vosoritide to see if it can safely help children with hypochondroplasia grow faster. About 80 children aged 3 to 17 with a confirmed genetic diagnosis and very short stature will receive either the drug or a placebo for one year. The main goal is to…
Matched conditions: HYPOCHONDROPLASIA
Phase: PHASE3 • Sponsor: BioMarin Pharmaceutical • Aim: Disease control
Last updated Jun 27, 2026 08:13 UTC
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Could a daily pill boost growth in kids with hypochondroplasia?
Disease control ENROLLING_BY_INVITATIONThis study tests an oral drug called infigratinib in children with hypochondroplasia, a condition that causes short stature. The trial has two parts: first, all children receive the drug to see if it safely increases their growth rate; then, some will switch to a placebo to confi…
Matched conditions: HYPOCHONDROPLASIA
Phase: PHASE2, PHASE3 • Sponsor: QED Therapeutics, a BridgeBio company • Aim: Disease control
Last updated Jun 27, 2026 08:04 UTC