HYPOCHONDROPLASIA
Clinical trials for HYPOCHONDROPLASIA explained in plain language.
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Experimental drug aims to help kids with genetic short stature grow taller
Disease control ENROLLING_BY_INVITATIONThis study is testing whether a drug called infigratinib can safely help children with hypochondroplasia, a genetic condition that causes short stature, grow faster and taller. It involves children aged 3 to 18 who have already been in a related observational study. The research …
Matched conditions: HYPOCHONDROPLASIA
Phase: PHASE2, PHASE3 • Sponsor: QED Therapeutics, a BridgeBio company • Aim: Disease control
Last updated Mar 30, 2026 14:32 UTC
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Extended trial tests growth drug for kids with rare genetic condition
Disease control ENROLLING_BY_INVITATIONThis study continues testing an experimental drug called infigratinib in children with hypochondroplasia, a genetic condition that causes short stature. It follows children who completed a previous study to monitor the drug's long-term safety and whether it helps with growth and …
Matched conditions: HYPOCHONDROPLASIA
Phase: PHASE2 • Sponsor: QED Therapeutics, a BridgeBio company • Aim: Disease control
Last updated Mar 25, 2026 14:09 UTC
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New hope for kids with genetic short stature: daily shot aims to boost growth
Disease control OngoingThis study is testing whether a daily injection called vosoritide can safely help children with hypochondroplasia grow taller. About 80 children, aged 3 to 18, will receive either the real drug or a placebo (a dummy injection) for one year to see which group grows faster. The mai…
Matched conditions: HYPOCHONDROPLASIA
Phase: PHASE3 • Sponsor: BioMarin Pharmaceutical • Aim: Disease control
Last updated Mar 20, 2026 14:48 UTC