GENE THERAPY
Clinical trials for GENE THERAPY explained in plain language.
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New gene therapy aims to rebuild immune system in 'Bubble Boy' disease
Disease control Recruiting nowThis study is testing a one-time gene therapy for young children with SCID-X1, a life-threatening genetic disorder where the immune system doesn't work. Doctors will collect the child's own blood stem cells, fix the faulty gene in a lab, and then infuse the corrected cells back a…
Matched conditions: GENE THERAPY
Phase: PHASE1, PHASE2 • Sponsor: David Williams • Aim: Disease control
Last updated Apr 01, 2026 14:42 UTC
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One-Shot gene therapy trial offers hope for Hard-to-Treat blood cancer
Disease control Recruiting nowThis early-stage trial is testing the safety of a new gene therapy called KLN-1010 for people with multiple myeloma that has returned after multiple treatments. The therapy aims to reprogram the patient's own immune cells inside their body to attack cancer cells. Researchers will…
Matched conditions: GENE THERAPY
Phase: PHASE1 • Sponsor: Kelonia Therapeutics, Inc. • Aim: Disease control
Last updated Mar 13, 2026 15:05 UTC