GAUCHER DISEASE
Clinical trials for GAUCHER DISEASE explained in plain language.
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Real-World check on gaucher disease drug shows promise
Disease control CompletedThis study aimed to monitor the real-world safety and effectiveness of the drug VPRIV (velaglucerase alfa) in patients with Gaucher disease in Japan. It followed 63 patients, including those new to treatment and those switching from other therapies. The main goal was to track sid…
Matched conditions: GAUCHER DISEASE
Sponsor: Takeda • Aim: Disease control
Last updated Mar 16, 2026 15:26 UTC
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Blood test aims to solve mystery of unexplained enlarged spleens
Diagnosis CompletedThis study aimed to find better ways to diagnose two rare genetic diseases, Gaucher disease and ASMD, in people with an enlarged spleen of unknown cause. Researchers enrolled 122 adult patients who had an unexplained enlarged spleen or had their spleen removed without a clear dia…
Matched conditions: GAUCHER DISEASE
Sponsor: Fundación Española de Hematología y Hemoterapía • Aim: Diagnosis
Last updated Apr 01, 2026 14:43 UTC
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Scientists scan brains to unlock link between two diseases
Knowledge-focused CompletedThis study aimed to understand the connection between Gaucher disease and Parkinson's disease by looking at how the brain works. Researchers used PET and MRI brain scans to compare people with these conditions, their family members, and healthy volunteers. The goal was to learn a…
Matched conditions: GAUCHER DISEASE
Sponsor: National Human Genome Research Institute (NHGRI) • Aim: Knowledge-focused
Last updated Mar 27, 2026 12:38 UTC