FANCONI ANEMIA
Clinical trials for FANCONI ANEMIA explained in plain language.
Never miss a new study
Get alerted when new FANCONI ANEMIA trials appear
Sign up with your email to follow new studies for FANCONI ANEMIA, keep track of the ones that matter, and come back to a personal dashboard instead of checking manually.
By submitting, you agree to our Terms of use
-
Gene therapy for rare blood disease shows promise in Long-Term Follow-Up
Disease control OngoingThis study checks on the long-term safety and effectiveness of a gene therapy for people with Fanconi Anemia, a rare genetic disorder that affects the bone marrow. Nine patients who received the therapy in an earlier study will be followed for 15 years to see if their blood count…
Matched conditions: FANCONI ANEMIA
Sponsor: Rocket Pharmaceuticals Inc. • Aim: Disease control
Last updated May 17, 2026 03:15 UTC
-
Gene therapy for rare blood disease shows promise in Long-Term Follow-Up
Disease control ENROLLING_BY_INVITATIONThis study checks the long-term safety and effectiveness of a gene therapy called RP-L102 for people with Fanconi Anemia, a rare genetic condition that causes bone marrow failure and raises cancer risk. About 14 patients who already received RP-L102 in earlier studies will be fol…
Matched conditions: FANCONI ANEMIA
Sponsor: Rocket Pharmaceuticals Inc. • Aim: Disease control
Last updated Apr 29, 2026 15:04 UTC
-
Glow-in-the-Dark mouth scans could catch cancer early
Diagnosis OngoingThis study tests whether special lights and cameras can help find early signs of mouth cancer in people at high risk. About 338 participants with mouth lesions or conditions like Fanconi anemia will have their mouths examined with fluorescence imaging and tissue sampling. The goa…
Matched conditions: FANCONI ANEMIA
Phase: NA • Sponsor: M.D. Anderson Cancer Center • Aim: Diagnosis
Last updated May 17, 2026 03:08 UTC