FANCONI ANEMIA

Clinical trials for FANCONI ANEMIA explained in plain language.

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Trials to join now! 10 Not yet recruiting 2 Not yet finished but already full! 1 Completed 1

First step toward a gene cure for devastating childhood blood disease

Disease control Completed

This small, early-stage study tested whether doctors could safely collect enough stem cells from the blood of children with Fanconi anemia. The goal was to see if these cells could then be used in a future gene therapy treatment. Researchers used two drugs to move stem cells from…

Matched conditions: FANCONI ANEMIA

Phase: PHASE1, PHASE2 • Sponsor: Assistance Publique - Hôpitaux de Paris • Aim: Disease control

Last updated Mar 31, 2026 12:10 UTC

FANCONI ANEMIA

Get alerted when new FANCONI ANEMIA trials appear

First step toward a gene cure for devastating childhood blood disease