FANCONI ANEMIA
Clinical trials for FANCONI ANEMIA explained in plain language.
Never miss a new study
Get alerted when new FANCONI ANEMIA trials appear
Sign up with your email to follow new studies for FANCONI ANEMIA, keep track of the ones that matter, and come back to a personal dashboard instead of checking manually.
By submitting, you agree to our Terms of use
-
Could a natural compound in apples prevent cancer in rare disease patients?
Prevention CompletedThis study tested whether quercetin, a natural compound found in fruits and vegetables, can prevent or delay squamous cell carcinoma (a type of mouth cancer) in people with Fanconi anemia, a rare genetic disorder that raises cancer risk. 48 participants took quercetin pills, and …
Matched conditions: FANCONI ANEMIA
Phase: PHASE2 • Sponsor: Children's Hospital Medical Center, Cincinnati • Aim: Prevention
Last updated May 15, 2026 11:54 UTC
-
Small study paves way for gene therapy in rare childhood disease
Knowledge-focused CompletedThis early-stage study tested whether a combination of two drugs (G-CSF and plerixafor) can safely collect enough blood stem cells from children with Fanconi anemia for future gene therapy. Only 4 children took part, and the main goal was to see if the cell collection was possibl…
Matched conditions: FANCONI ANEMIA
Phase: PHASE1, PHASE2 • Sponsor: Assistance Publique - Hôpitaux de Paris • Aim: Knowledge-focused
Last updated May 14, 2026 12:06 UTC