FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY
Clinical trials for FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY explained in plain language.
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Breakthrough drug trial offers hope for rare muscle disease
Disease control Recruiting nowThis study is testing an experimental drug called AOC 1020 for people with facioscapulohumeral muscular dystrophy (FSHD), a genetic condition that causes progressive muscle weakness. About 200 participants will receive either the drug or a placebo via IV infusion every six weeks …
Matched conditions: FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY
Phase: PHASE3 • Sponsor: Avidity Biosciences, Inc. • Aim: Disease control
Last updated Mar 30, 2026 14:32 UTC
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Scientists test One-Shot gene therapy to silence root cause of Muscle-Wasting disease
Disease control Recruiting nowThis early-stage study is testing a new, one-time gene therapy called EPI-321 in adults with FSHD, a genetic muscle-wasting disease. The main goal is to find out if the treatment is safe and what dose is best, while also looking for early signs that it might be working. About 12 …
Matched conditions: FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY
Phase: PHASE1, PHASE2 • Sponsor: Epicrispr Biotechnologies, Inc. • Aim: Disease control
Last updated Mar 10, 2026 12:53 UTC
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Researchers seek simple tests to replace painful muscle biopsies
Knowledge-focused Recruiting nowThis study aims to find easier ways to measure muscular dystrophy disease activity. Researchers will collect urine and blood samples and use painless scans on the arms and legs of about 465 participants. The goal is to see if these simple tests can work as well as or better than …
Matched conditions: FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY
Sponsor: Massachusetts General Hospital • Aim: Knowledge-focused
Last updated Apr 02, 2026 00:27 UTC
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National registry opens doors for rare muscle disease research
Knowledge-focused Recruiting nowThis study creates a national registry to connect people with myotonic dystrophy or facioscapulohumeral muscular dystrophy (FSHD) with researchers. It aims to better understand these rare muscle diseases by tracking symptoms over time and helping match interested participants to …
Matched conditions: FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY
Sponsor: University of Rochester • Aim: Knowledge-focused
Last updated Mar 30, 2026 14:34 UTC
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Patients unite to power FSHD research through new national registry
Knowledge-focused Recruiting nowBetterLife FSHD is a patient-driven registry and online platform for people with Facioscapulohumeral Muscular Dystrophy (FSHD). It aims to collect health and experience data from up to 5,000 participants through regular surveys to help researchers better understand the disease. T…
Matched conditions: FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY
Sponsor: FSHD Society • Aim: Knowledge-focused
Last updated Mar 13, 2026 15:06 UTC