FABRY DISEASE
Clinical trials for FABRY DISEASE explained in plain language.
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New Real-World study tracks fabry Drug's Long-Term impact on heart and kidneys
Disease control Not yet recruitingThis study follows 75 adults with Fabry disease who are taking or starting pegunigalsidase alfa to see how well it works and how safe it is over time in real-world settings. Researchers will check heart structure and function, kidney health, and exercise capacity. The goal is to …
Matched conditions: FABRY DISEASE
Sponsor: Chiesi Italia • Aim: Disease control
Last updated Jun 10, 2026 13:26 UTC
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Untreated fabry patients share their stories in new study
Knowledge-focused Not yet recruitingThis study aims to learn how adults with Fabry disease who are not yet receiving treatment experience their quality of life, daily activities, and healthcare support. Researchers will interview 35 participants in Sweden for about an hour each. The goal is to identify unmet needs …
Matched conditions: FABRY DISEASE
Sponsor: Vastra Gotaland Region • Aim: Knowledge-focused
Last updated Jun 16, 2026 23:59 UTC
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New clues to heart risk in rare fabry disease
Knowledge-focused Not yet recruitingThis study aims to find new biological markers and imaging techniques to better understand and predict heart problems in people with Fabry disease. Researchers will analyze heart tissue samples and blood tests from 20 adult patients. The goal is to improve diagnosis and risk asse…
Matched conditions: FABRY DISEASE
Sponsor: Núcleo de Apoio à Investigação Clínica - FMUP • Aim: Knowledge-focused
Last updated Jun 15, 2026 18:57 UTC
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Rare kidney disease Patients' gum health under microscope
Knowledge-focused Not yet recruitingThis study looks at how common and severe gum disease is in people with rare kidney disorders like Alport syndrome, Fabry disease, and tuberous sclerosis, as well as lupus with kidney involvement. Researchers will compare them to people with chronic kidney disease and healthy vol…
Matched conditions: FABRY DISEASE
Sponsor: Stefan Lujinschi • Aim: Knowledge-focused
Last updated Jun 10, 2026 13:25 UTC
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Fabry disease study aims to close gender gap in diagnosis
Knowledge-focused Not yet recruitingThis study looks at how men and women with Fabry disease are diagnosed and treated. Fabry disease affects men and women differently, and women are often diagnosed later or through family screening. Researchers will survey 200 adults with Fabry disease to compare their care paths …
Matched conditions: FABRY DISEASE
Sponsor: University Hospital, Toulouse • Aim: Knowledge-focused
Last updated May 26, 2026 12:05 UTC