FABRY DISEASE

Clinical trials for FABRY DISEASE explained in plain language.

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Trials to join now! 5 Not yet finished but already full! 2 Completed 1

Gene therapy aims to fix fabry disease with one infusion

Disease control Completed

This study tested a new gene therapy called ST-920 in 36 adults with Fabry disease. The treatment uses a harmless virus to deliver a working gene that helps the body produce an enzyme it is missing. The goal was to see if a single intravenous dose is safe and tolerable, and wheth…

Matched conditions: FABRY DISEASE

Phase: PHASE1, PHASE2 • Sponsor: Sangamo Therapeutics • Aim: Disease control

Last updated Apr 28, 2026 13:02 UTC

FABRY DISEASE

Get alerted when new FABRY DISEASE trials appear

Gene therapy aims to fix fabry disease with one infusion