Trial seeks cheaper alternative for rare disease patients

NCT ID NCT05843916

Summary

This study tested if a new, potentially more affordable version of an existing Fabry disease drug works as well and is as safe. It involved 20 adult patients who were already stable on the standard treatment, Fabrazyme. For one year, researchers monitored if switching them to the new drug, AGA BETA BS, kept their disease under control by checking blood markers, pain levels, and heart and kidney health.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

Get updates

Get notified about this study

Sign up to get updates when this study changes or when new studies for FABRY DISEASE are added.

Our safety recommendation!

By submitting, you agree to our Terms of use

Contacts and locations

Locations

  • Centro Médico Santa María de la Salud

    San Isidro, Buenos Aires, 1642, Argentina

  • Centro Oncológico Riojano Integral

    La Rioja, F5300, Argentina

  • Clínica Universitaria Reina Fabiola

    Córdoba, X5004, Argentina

  • Instituto de Investigaciones Clínicas Quilmes

    Buenos Aires, Argentina

  • Instituto de Nefrología Pergamino S.R.L

    Pergamino, Buenos Aires, 2700, Argentina

Conditions

Explore the condition pages connected to this study.