CYSTINOSIS
Clinical trials for CYSTINOSIS explained in plain language.
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Cystinosis drug under Long-Term watch: could cysteamine be key?
Disease control Recruiting nowCystinosis is a rare inherited disease that causes kidney failure and poor growth due to cystine buildup in cells. This study follows 330 patients taking cysteamine, a drug that lowers cystine levels, to track long-term effects, detect new complications, and support genetic resea…
Matched conditions: CYSTINOSIS
Sponsor: National Human Genome Research Institute (NHGRI) • Aim: Disease control
Last updated Jul 30, 2026 00:00 UTC
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Scientists investigate why cystinosis causes early aging
Knowledge-focused Recruiting nowThis study looks at how energy production inside cells (mitochondria) works in people with cystinosis, a rare disease that causes cystine buildup and early aging. Researchers will measure cell energy activity in 25 patients and compare it to healthy people. The goal is to underst…
Matched conditions: CYSTINOSIS
Phase: NA • Sponsor: Hospices Civils de Lyon • Aim: Knowledge-focused
Last updated Aug 05, 2026 00:00 UTC
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Rare disease database aims to boost cystinosis care across europe
Knowledge-focused Recruiting nowThis European study will follow 400 people with cystinosis, a rare genetic disease that causes cystine buildup in cells. Researchers will collect medical and quality-of-life data to understand how the disease progresses and how care can be improved. The study does not test any ne…
Matched conditions: CYSTINOSIS
Sponsor: Institut National de la Santé Et de la Recherche Médicale, France • Aim: Knowledge-focused
Last updated Jul 09, 2026 00:00 UTC