ALPERS SYNDROME

Clinical trials for ALPERS SYNDROME explained in plain language.

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Not yet finished but already full! 1 Completed 1 Terminated 1

Long-Term safety of mitochondrial drug confirmed in 101 patients

Disease control Completed

This study looked at the safety of vatiquinone in 101 people with inherited mitochondrial disease who had already taken the drug in a previous study or treatment plan. The goal was to track any side effects until the drug became commercially available or the program ended. Partic…

Matched conditions: ALPERS SYNDROME

Phase: PHASE3 • Sponsor: PTC Therapeutics • Aim: Disease control

Last updated Jun 27, 2026 08:05 UTC

ALPERS SYNDROME

Get alerted when new ALPERS SYNDROME trials appear

Long-Term safety of mitochondrial drug confirmed in 101 patients