ALPERS SYNDROME

Clinical trials for ALPERS SYNDROME explained in plain language.

Never miss a new study

Get alerted when new ALPERS SYNDROME trials appear

Sign up with your email to follow new studies for ALPERS SYNDROME, keep track of the ones that matter, and come back to a personal dashboard instead of checking manually.

Our safety recommendation!

By submitting, you agree to our Terms of use

Not yet finished but already full! 1 Completed 1 Terminated 1

New drug aims to tame hard-to-control seizures in rare mitochondrial disorders

Disease control Terminated

This study tested a drug called vatiquinone in 68 people with mitochondrial disease and epilepsy that doesn't respond to standard treatments. Participants were randomly assigned to receive either vatiquinone or a placebo for 24 weeks to see if the drug could reduce the number of …

Matched conditions: ALPERS SYNDROME

Phase: PHASE2, PHASE3 • Sponsor: PTC Therapeutics • Aim: Disease control

Last updated Jun 27, 2026 12:03 UTC

ALPERS SYNDROME

Get alerted when new ALPERS SYNDROME trials appear

New drug aims to tame hard-to-control seizures in rare mitochondrial disorders