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Search the conditions that have clinical trials.
7535 conditions with clinical trials.
- Methylmalonic aciduria and homocystinuria type cblF 1 trial · 22 incl. sub-types
- Multiple acyl-CoA dehydrogenase deficiency 1 trial · 22 incl. sub-types
- Pulmonary hypertension, neonatal 1 trial · 22 incl. sub-types
- Regional odontodysplasia 1 trial · 22 incl. sub-types
- Syndromic craniosynostosis 1 trial · 22 incl. sub-types
- Amaurosis fugax 1 trial · 21 incl. sub-types
- Hereditary intrinsic factor deficiency 1 trial · 21 incl. sub-types
- Lafora disease 1 trial · 21 incl. sub-types
- Neurodegeneration with brain iron accumulation 1 trial · 21 incl. sub-types
- Pernicious anemia 1 trial · 21 incl. sub-types
- Pyruvate dehydrogenase E3 deficiency 1 trial · 21 incl. sub-types
- Spinocerebellar ataxia 27A 1 trial · 21 incl. sub-types
- Transcobalamin II deficiency 1 trial · 21 incl. sub-types
- Autosomal dominant progressive external ophthalmoplegia 1 trial · 20 incl. sub-types
- Bacillaceae infectious disease 1 trial · 20 incl. sub-types
- Paraneoplastic syndrome 1 trial · 20 incl. sub-types
- Progressive external ophthalmoplegia with mitochondrial DNA deletions, autosomal dominant 2 1 trial · 20 incl. sub-types
- Spinocerebellar ataxia type 23 1 trial · 20 incl. sub-types
- Spinocerebellar ataxia type 29 1 trial · 20 incl. sub-types
- Unverricht-Lundborg syndrome 1 trial · 20 incl. sub-types
- Adenosine monophosphate deaminase deficiency 1 trial · 19 incl. sub-types
- Autosomal recessive limb-girdle muscular dystrophy type R18 1 trial · 19 incl. sub-types
- Autosomal recessive spinocerebellar ataxia 7 1 trial · 19 incl. sub-types
- Charlevoix-Saguenay spastic ataxia 1 trial · 19 incl. sub-types
- COACH syndrome 1 trial · 19 incl. sub-types
- Developmental and epileptic encephalopathy, 42 1 trial · 19 incl. sub-types
- Developmental and epileptic encephalopathy 94 1 trial · 19 incl. sub-types
- Friedreich ataxia 1 1 trial · 19 incl. sub-types
- Joubert syndrome with oculorenal defect 1 trial · 19 incl. sub-types
- Maternally-inherited Leigh syndrome 1 trial · 19 incl. sub-types
- MELAS syndrome caused by mutation in MTTL1 1 trial · 19 incl. sub-types
- Partial retinal vein occlusion 1 trial · 19 incl. sub-types
- Retinal microaneurysm 1 trial · 19 incl. sub-types
- Developmental and epileptic encephalopathy 114 1 trial · 18 incl. sub-types
- Developmental and epileptic encephalopathy, 25 1 trial · 18 incl. sub-types
- Developmental and epileptic encephalopathy, 35 1 trial · 18 incl. sub-types
- Developmental and epileptic encephalopathy, 7 1 trial · 18 incl. sub-types
- Esophageal leukoplakia 1 trial · 18 incl. sub-types
- Hereditary hypophosphatemic rickets 1 trial · 18 incl. sub-types
- Megaloblastic anemia 1 trial · 18 incl. sub-types
- Non-neonatal early infantile epileptic encephalopathy 1 trial · 18 incl. sub-types
- Carotid artery thrombosis 1 trial · 17 incl. sub-types
- Hearing loss, autosomal recessive 1 trial · 17 incl. sub-types
- Histoplasmosis retinitis 1 trial · 17 incl. sub-types
- Paroxysmal dyskinesia 1 trial · 17 incl. sub-types
- Peripheral nerve lesion 1 trial · 17 incl. sub-types
- Sickle cell disease due to hemoglobin S and a non-S/non-C hemoglobin variant 1 trial · 17 incl. sub-types
- Sudden unexpected death in pediatrics 1 trial · 17 incl. sub-types
- Atypical progressive supranuclear palsy syndrome 1 trial · 16 incl. sub-types
- Coloboma of optic nerve 1 trial · 16 incl. sub-types