Experimental eye injection targets rare Blindness-Causing gene
NCT ID NCT06455826
First seen Apr 16, 2026 · Last updated May 24, 2026 · Updated 9 times
Summary
This early-stage study tested a new drug called VP-001 in 6 people with a rare inherited eye disease caused by a PRPF31 gene mutation. The drug was given as an injection into the eye to see if it is safe and tolerable. The goal was to check for side effects, not to measure if it improves vision.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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Baylor College of Medicine- Alkek Eye Center
Houston, Texas, 77030, United States
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Oregon Health and Science University - Casey Eye Institute
Portland, Oregon, 97239, United States
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Retina Foundation of the Southwest
Dallas, Texas, 75321, United States
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University of Florida Health
Jacksonville, Florida, 32209, United States
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University of Michigan Kellogg Eye Center
Ann Arbor, Michigan, 48105, United States
Conditions
Explore the condition pages connected to this study.