New hope for rare blood vessel disorder: targeted drug shows promise
NCT ID NCT04258046
First seen May 02, 2026 · Last updated Jun 17, 2026 · Updated 9 times
Summary
This study tested the drug trametinib in 25 people aged 12 to 60 with complicated arteriovenous malformations (AVMs), which are abnormal blood vessel tangles that can cause pain, bleeding, and heart problems. The goal was to see if the drug could shrink the malformations and improve symptoms. Participants took trametinib pills daily, and doctors monitored their response using scans and quality-of-life measures.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Genom att skicka in godkänner du våra Användarvillkor
Contacts and locations
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Locations
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Pediatric Dermatology Clinic at Stanford Children's Hospital
Palo Alto, California, 94304, United States
Conditions
The condition(s) this trial relates to.
As listed by the trial registrant
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