New drug shows promise for rare, destructive blood vessel disorder
NCT ID NCT04258046
First seen May 02, 2026 · Last updated May 08, 2026 · Updated 2 times
Summary
This study tested the drug trametinib in 25 people aged 12 to 60 with complicated arteriovenous malformations (AVMs)—abnormal blood vessel tangles that can cause bleeding, pain, and heart problems. The goal was to see if the drug could shrink the malformations and improve symptoms. Participants took trametinib by mouth, and doctors monitored their response using scans and quality-of-life measures.
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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Locations
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Pediatric Dermatology Clinic at Stanford Children's Hospital
Palo Alto, California, 94304, United States
Conditions
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