Can a stem cell transplant slow this rare brain disease?
NCT ID NCT04503213
First seen Oct 31, 2025 · Last updated May 23, 2026 · Updated 32 times
Summary
This study looks at whether a stem cell transplant can help people with a rare genetic brain disease called CSF1R-related leukoencephalopathy. Researchers will track changes in thinking and movement skills in 20 adults who are already scheduled for the transplant. The goal is to see if the procedure can stabilize or improve symptoms.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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Mayo Clinic in Florida
Jacksonville, Florida, 32224, United States
Conditions
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