Sugar therapy faces its biggest test yet for rare disease
NCT ID NCT05402332
First seen Nov 01, 2025 · Last updated May 20, 2026 · Updated 29 times
Summary
This study tests if a sugar called AVTX-801 (D-galactose) can help control symptoms of a rare genetic disease called PGM1-CDG. About 8 adults who already take D-galactose will be randomly assigned to get the study drug or a placebo, then switch. The goal is to see if it reduces episodes of low blood sugar, liver stress, or blood clotting problems.
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the original study
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Genom att skicka in godkänner du våra Användarvillkor
Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Mayo Clinic Rochester
Rochester, Minnesota, 55905, United States
Conditions
Explore the condition pages connected to this study.