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PGM1-CDG - phosphoglucomutase 1-related congenital disorder of glycosylation

Clinical trials for PGM1-CDG - phosphoglucomutase 1-related congenital disorder of glycosylation explained in plain language.

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Sugar supplement shows promise for rare disease in new trial

Disease control Not yet recruiting

This phase 2b trial tests AVTX-801, a D-galactose supplement, in 8 adults with PGM1-CDG, a rare genetic disorder affecting sugar metabolism. Participants currently on D-galactose will receive either the study drug or a placebo to see if it reduces disease-related events like low …

Matched conditions: PGM1-CDG - PHOSPHOGLUCOMUTASE 1-RELATED CONGENITAL DISORDER OF GLYCOSYLATION

Phase 2 • Sponsor: Eva Morava-Kozicz • Aim: Disease control

Last updated Jun 27, 2026 11:01 UTC

PGM1-CDG - phosphoglucomutase 1-related congenital disorder of glycosylation

Get alerted when new PGM1-CDG - phosphoglucomutase 1-related congenital disorder of glycosylation trials appear

Sugar supplement shows promise for rare disease in new trial