SMA treatments reveal new disease patterns – scientists investigate
NCT ID NCT06321965
First seen Jan 30, 2026 · Last updated May 25, 2026 · Updated 20 times
Summary
This study follows 60 children with spinal muscular atrophy (SMA) who are already receiving SMN-restoring therapies like nusinersen or gene therapy. Researchers want to describe the new disease patterns that emerge with these treatments and find better ways to monitor progress. The goal is to improve care and design smarter future clinical trials.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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CHRU of Brest
NOT_YET_RECRUITINGBrest, 29609, France
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact
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Department of Pediatrics - Neurology and Infectious Diseases Toulouse University Hospital - Children's Hospital
NOT_YET_RECRUITINGToulouse, 31059, France
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact
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Hautepierre Hospital - Mother and Child Hospital
NOT_YET_RECRUITINGStrasbourg, 67200, France
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact
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I-Motion Pediatric Clinical Trial Platform Armand Trousseau Hospital
NOT_YET_RECRUITINGParis, 75012, France
Contact
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Marseille University Hospital - Timone Hospital Department of Pediatric Neurology - Specialized Pediatrics and Child Medicine
NOT_YET_RECRUITINGMarseille, 13005, France
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact
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Pediatric Neurology Swynghedauw Hospital
NOT_YET_RECRUITINGLille, 59037, France
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact
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Pediatric Neurology and Resuscitation Raymond-Poincare Hospital
NOT_YET_RECRUITINGGarche, 92380, France
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact
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Pediatric Rehabilitation Service - L'Escale Mother and Child Hospital
RECRUITINGBron, Rhone, 69500, France
Contact
Contact Phone: •••-•••-•••• Email: •••••@•••••
Conditions
Explore the condition pages connected to this study.