Major trial tests new IV drug for debilitating muscle disease
NCT ID NCT06411288
Summary
This study is testing whether an intravenous drug called AOC 1001 can improve muscle function and control symptoms in adults with myotonic dystrophy type 1 (DM1). Participants receive either the drug or a placebo via infusion every 8 weeks for about a year. The main goal is to see if the treatment helps with hand function, strength, and walking ability.
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Contacts and locations
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Locations
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AP-HP Hopital Pitie-Salpetriere
Paris, 75013, France
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Aarhus University Hospital
Aarhus N, 8200, Denmark
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Aomori Hospital
Aomori, Aomori, 038-1331, Japan
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Beth Israel Deaconess Medical Center
Boston, Massachusetts, 02215, United States
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Duke University Medical Center
Durham, North Carolina, 27708, United States
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Fondazione Serena Onlus - Centro Clinico NeMO Milano
Milan, 20162, Italy
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Hospital Universitario Donostia
Donostia / San Sebastian, 20014, Spain
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Houston Methodist Neurological Institute
Houston, Texas, 77030, United States
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Indiana University (IU)
Indianapolis, Indiana, 46202, United States
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Kansas University Medical Center
Kansas City, Kansas, 66205, United States
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Kennedy Krieger Institute
Baltimore, Maryland, 21205, United States
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Klinikum der Ludwig-Maximilians-Universitaet Muenchen
Munich, 80336, Germany
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Maastricht University Medical Center
Maastricht, 6229 HX, Netherlands
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Montreal Neurological Institute
Montreal, Quebec, H3A 2B4, Canada
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National Center of Neurology and Psychiatry
Tokyo, 187-8551, Japan
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National Hospital Organization Osaka Toneyama Medical Center
Osaka, 560-8552, Japan
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Ohio State University
Columbus, Ohio, 43221, United States
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Osaka University Hospital
Osaka, 565-0871, Japan
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Rigshospitalet
Copenhagen, 2100, Denmark
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St. Georges University Hospitals NHS Foundation Trust
London, SW17 0QT, United Kingdom
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Stanford University
Stanford, California, 94305, United States
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Stichting Radboud Universitair Medisch Centrum
Nijmegen, 6525 GA, Netherlands
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The Ottawa Hospital
Ottawa, Ontario, K1Y 4E9, Canada
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University College London Hospital
London, NW1 2BU, United Kingdom
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University Research Center of South Florida
Tampa, Florida, 33612, United States
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University of Cincinnati Gardner Neuroscience Institute
Cincinnati, Ohio, 45219, United States
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University of Colorado
Denver, Colorado, 80045, United States
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University of Florida
Gainesville, Florida, 32608, United States
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University of Minnesota
Minneapolis, Minnesota, 55455, United States
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University of Pennsylvania
Philadelphia, Pennsylvania, 19104, United States
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University of Rochester Medical Center
Rochester, New York, 14642, United States
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University of Washington
Seattle, Washington, 98104, United States
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Virginia Commonwealth University
Richmond, Virginia, 23298, United States
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Wake Forest
Winston-Salem, North Carolina, 27157, United States
Conditions
Explore the condition pages connected to this study.