New hope for kids with dwarfism: daily pill may boost growth
NCT ID NCT05145010
First seen Nov 01, 2025 · Last updated May 23, 2026 · Updated 29 times
Summary
This study tests a daily pill called infigratinib in children with achondroplasia, the most common form of dwarfism. The goal is to see if it safely improves growth over several years. About 300 children who were in earlier studies or are new to the drug will take part. Because treatment is ongoing, this is a disease-control approach, not a cure.
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This is a summary of
the original study
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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Birmingham Women's and Children's NHS Foundation Trust
Birmingham, B5 6NH, United Kingdom
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Centre Hospitalier Universitaire Sainte-Justine
Montreal, Quebec, H3T 1C5, Canada
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Children's Hospital - London Health Sciences Centre
London, Ontario, N6A 5W9, Canada
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Children's Hospital Colorado
Aurora, Colorado, 80045, United States
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Children's Hospital of Eastern Ontario
Ottawa, Ontario, K1H 8L1, Canada
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Cincinnati Children's Hospital Medical Center
Cincinnati, Ohio, 45229, United States
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Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico
Milan, 20122, Italy
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Haukeland University Hospital
Bergen, 5021, Norway
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Hopital Femme Mere Enfant
Lyon, 69500, France
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Hopital Necker-Enfants Malades
Paris, 75743, France
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Hopital des Enfants
Toulouse, 31300, France
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Hospital Universitario La Paz
Madrid, 28046, Spain
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Hospital Universitario Virgen de la Victoria
Málaga, 29010, Spain
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Hospital Vithas San José
Vitoria-Gasteiz, Álava, 01012, Spain
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Hospital de Pediatría SAMIC Prof. Dr. Juan P. Garrahan
Ciudad Autonoma Buenos Aires, Buenos Aires, C1245AAM, Argentina
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Johns Hopkins University
Baltimore, Maryland, 21205, United States
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KK Women's and Children's Hosptial
Singapore, 229899, Singapore
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Manchester University Children's Hospital
Manchester, M13 9WL, United Kingdom
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Murdoch Children's Hospital
Parkville, Victoria, 3052, Australia
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Nemours Alfred I. Dupont Hospital for Children
Wilmington, Delaware, 19803, United States
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Oslo University Hospital
Oslo, 0372, Norway
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Policlinico A. Gemelli IRCCS
Roma, 00168, Italy
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Queen Elizabeth University Hospital
Glasgow, G12 0XH, United Kingdom
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Sheffield Children's Hospital
Sheffield, S10 2TH, United Kingdom
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St. Thomas' Hospital
London, SE1 7EH, United Kingdom
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Stollery Children's Hospital
Edmonton, Alberta, T6C 2B7, Canada
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USCF Benioff Children's Hospital, Oakland
Oakland, California, 94609, United States
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University Hospital and UW Health Clinics
Madison, Wisconsin, 53705, United States
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University Hospitals Bristol and Weston NHS Foundation Trust
Bristol, BS2 8AE, United Kingdom
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University of Missouri
Columbia, Missouri, 65212, United States
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Vanderbilt University Medical Center
Nashville, Tennessee, 37232, United States
Conditions
Explore the condition pages connected to this study.