Daily pill aims to help kids with dwarfism grow taller and healthier

NCT ID NCT05145010

Summary

This study is testing the long-term safety and effectiveness of a daily oral medication called infigratinib in children with achondroplasia, the most common form of dwarfism. It aims to see if the drug can help children grow taller at a rate closer to average, improve their body proportions, and reduce common health problems. The study is open to children aged 3 to 18 who have growth potential and have either been in a previous related study or meet specific new criteria.

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Contacts and locations

Locations

  • Birmingham Women's and Children's NHS Foundation Trust

    Birmingham, B5 6NH, United Kingdom

  • Centre Hospitalier Universitaire Sainte-Justine

    Montreal, Quebec, H3T 1C5, Canada

  • Children's Hospital - London Health Sciences Centre

    London, Ontario, N6A 5W9, Canada

  • Children's Hospital Colorado

    Aurora, Colorado, 80045, United States

  • Children's Hospital of Eastern Ontario

    Ottawa, Ontario, K1H 8L1, Canada

  • Cincinnati Children's Hospital Medical Center

    Cincinnati, Ohio, 45229, United States

  • Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico

    Milan, 20122, Italy

  • Haukeland University Hospital

    Bergen, 5021, Norway

  • Hopital Femme Mere Enfant

    Lyon, 69500, France

  • Hopital Necker-Enfants Malades

    Paris, 75743, France

  • Hopital des Enfants

    Toulouse, 31300, France

  • Hospital Universitario La Paz

    Madrid, 28046, Spain

  • Hospital Universitario Virgen de la Victoria

    Málaga, 29010, Spain

  • Hospital Vithas San José

    Vitoria-Gasteiz, Álava, 01012, Spain

  • Hospital de Pediatría SAMIC Prof. Dr. Juan P. Garrahan

    Ciudad Autonoma Buenos Aires, Buenos Aires, C1245AAM, Argentina

  • Johns Hopkins University

    Baltimore, Maryland, 21205, United States

  • KK Women's and Children's Hosptial

    Singapore, 229899, Singapore

  • Manchester University Children's Hospital

    Manchester, M13 9WL, United Kingdom

  • Murdoch Children's Hospital

    Parkville, Victoria, 3052, Australia

  • Nemours Alfred I. Dupont Hospital for Children

    Wilmington, Delaware, 19803, United States

  • Oslo University Hospital

    Oslo, 0372, Norway

  • Policlinico A. Gemelli IRCCS

    Roma, 00168, Italy

  • Queen Elizabeth University Hospital

    Glasgow, G12 0XH, United Kingdom

  • Sheffield Children's Hospital

    Sheffield, S10 2TH, United Kingdom

  • St. Thomas' Hospital

    London, SE1 7EH, United Kingdom

  • Stollery Children's Hospital

    Edmonton, Alberta, T6C 2B7, Canada

  • USCF Benioff Children's Hospital, Oakland

    Oakland, California, 94609, United States

  • University Hospital and UW Health Clinics

    Madison, Wisconsin, 53705, United States

  • University Hospitals Bristol and Weston NHS Foundation Trust

    Bristol, BS2 8AE, United Kingdom

  • University of Missouri

    Columbia, Missouri, 65212, United States

  • Vanderbilt University Medical Center

    Nashville, Tennessee, 37232, United States

Conditions

Explore the condition pages connected to this study.