Gene therapy shows promise for rare eye disease
NCT ID NCT02064569
First seen Mar 14, 2026 · Last updated May 23, 2026 · Updated 12 times
Summary
This study tested the safety of a new gene therapy called GS010 for people with Leber Hereditary Optic Neuropathy (LHON), a genetic condition that causes sudden vision loss. Nineteen adults with a specific gene mutation received the treatment through an injection into the eye. The main goal was to see if different doses were safe and well-tolerated.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Genom att skicka in godkänner du våra Användarvillkor
Contacts and locations
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Genom att skicka in godkänner du våra Användarvillkor
Locations
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CIC du CHNO DES QUINZE-VINGTS
Paris, 75012, France
Conditions
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