Gene therapy skin patches offer hope for 'Butterfly Children'
NCT ID NCT04186650
First seen Feb 12, 2026 · Last updated Apr 30, 2026 · Updated 12 times
Summary
This early-stage trial tests a new gene therapy for people with a severe form of epidermolysis bullosa, a condition that causes fragile, blistering skin. Researchers take a small piece of the patient's own skin, fix the faulty gene in a lab, and grow it into a healthy skin patch that is grafted back onto the patient. The goal is to see if the procedure is safe and if the new skin can heal and stay strong without long-term side effects.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Genom att skicka in godkänner du våra Användarvillkor
Contacts and locations
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Genom att skicka in godkänner du våra Användarvillkor
Locations
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Institut Imagine Necker Hospital
Paris, 75743, France
Conditions
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