Experimental gene therapy aims to protect lungs in Alpha-1 patients
NCT ID NCT06996756
First seen Oct 31, 2025 · Last updated May 22, 2026 · Updated 31 times
Summary
This early-stage study tests a one-time gene therapy for alpha-1 antitrypsin deficiency, a genetic condition that can lead to lung damage. Researchers want to see if the treatment is safe and can raise protective protein levels in the blood. The study involves 16 adults with mild to moderate emphysema caused by this deficiency.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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WCMC Department of Genetic Medicine
RECRUITINGNew York, New York, 10021, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact
Contact Phone: •••-•••-•••• Email: •••••@•••••
Conditions
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