New hope for kids with relapsed leukemia: targeted pill shows promise
NCT ID NCT04203316
First seen Nov 01, 2025 · Last updated May 22, 2026 · Updated 31 times
Summary
This study looks at a drug called enasidenib for children and teens with acute myeloid leukemia (AML) that has returned or not responded to standard treatment. Only patients with a specific genetic change (IDH2 mutation) are included. The goal is to check the drug's safety and how the body processes it, with early signs of effectiveness also being measured.
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This is a summary of
the original study
.
Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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Alfred I duPont Hospital for Children
Wilmington, Delaware, 19803, United States
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Arkansas Children's Hospital
Little Rock, Arkansas, 72202-3591, United States
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C S Mott Children's Hospital
Ann Arbor, Michigan, 48109, United States
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Centre Hospitalier Universitaire Sainte-Justine
Montreal, Quebec, H3T 1C5, Canada
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Children's Hospital Colorado
Aurora, Colorado, 80045, United States
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Children's Hospital of Alabama
Birmingham, Alabama, 35233, United States
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Children's Hospital of Philadelphia
Philadelphia, Pennsylvania, 19104, United States
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Children's Hospital of Pittsburgh of UPMC
Pittsburgh, Pennsylvania, 15224, United States
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Children's Hospital of San Antonio
San Antonio, Texas, 78207, United States
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Children's Hospital of The King's Daughters
Norfolk, Virginia, 23507, United States
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Children's Mercy Hospitals and Clinics
Kansas City, Missouri, 64108, United States
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Children's National Medical Center
Washington D.C., District of Columbia, 20010, United States
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Cincinnati Children's Hospital Medical Center
Cincinnati, Ohio, 45229, United States
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Hackensack University Medical Center
Hackensack, New Jersey, 07601, United States
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Johns Hopkins University/Sidney Kimmel Cancer Center
Baltimore, Maryland, 21287, United States
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Lurie Children's Hospital-Chicago
Chicago, Illinois, 60611, United States
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MedStar Georgetown University Hospital
Washington D.C., District of Columbia, 20007, United States
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Montefiore Medical Center - Moses Campus
The Bronx, New York, 10467, United States
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Nicklaus Children's Hospital
Miami, Florida, 33155, United States
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Norton Children's Hospital
Louisville, Kentucky, 40202, United States
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Riley Hospital for Children
Indianapolis, Indiana, 46202, United States
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Rocky Mountain Hospital for Children-Presbyterian Saint Luke's Medical Center
Denver, Colorado, 80218, United States
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Saint Jude Children's Research Hospital
Memphis, Tennessee, 38105, United States
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State University of New York Upstate Medical University
Syracuse, New York, 13210, United States
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UF Health Cancer Institute - Gainesville
Gainesville, Florida, 32610, United States
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UT Southwestern/Simmons Cancer Center-Dallas
Dallas, Texas, 75390, United States
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University of Oklahoma Health Sciences Center
Oklahoma City, Oklahoma, 73104, United States
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Vanderbilt University/Ingram Cancer Center
Nashville, Tennessee, 37232, United States
Conditions
Explore the condition pages connected to this study.