Could this drug restore sight in friedreich ataxia?
NCT ID NCT05168774
First seen Jan 05, 2026 · Last updated May 25, 2026 · Updated 26 times
Summary
This study tested the safety and effectiveness of elamipretide for treating vision loss in people with Friedreich ataxia (FRDA). Twenty participants with advanced symptoms received either a low or high dose of the drug. The main goal was to see if it improved how many letters they could read on an eye chart.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Locations
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Children's Hospital of Philadelphia - Neurology
Philadelphia, Pennsylvania, 19104, United States
Conditions
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