Decades-Long study tracks rare disease treatment
NCT ID NCT00359684
Summary
This study follows patients with cystinosis, a rare inherited disease that causes kidney failure and poor growth, who are taking the medication cysteamine. Researchers monitor patients every two years to track how well the drug reduces cystine buildup in their bodies and to identify any new complications. The goal is to better understand the long-term effects of treatment and the natural course of this rare disease.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
Get updates
Get notified about this study
Sign up to get updates when this study changes or when new studies for CYSTINOSIS are added.
Genom att skicka in godkänner du våra Användarvillkor
Contacts and locations
Show contact details
Enter your email to view the contact information for this study.
Genom att skicka in godkänner du våra Användarvillkor
Study contacts
-
Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
-
National Institutes of Health Clinical Center
RECRUITINGBethesda, Maryland, 20892, United States
Conditions
Explore the condition pages connected to this study.