CYSTINOSIS
Clinical trials for CYSTINOSIS explained in plain language.
Never miss a new study
Get alerted when new CYSTINOSIS trials appear
Sign up with your email to follow new studies for CYSTINOSIS, keep track of the ones that matter, and come back to a personal dashboard instead of checking manually.
Genom att skicka in godkänner du våra Användarvillkor
-
New cystinosis drug shows promise in early trial
Disease control Recruiting nowThis study tests a new oral medicine called NPI-001 for people with cystinosis, a rare disease that causes cystine buildup in cells. It compares NPI-001 to the standard drug cysteamine in 12 patients aged 10 and older. The goal is to see if NPI-001 is safe and how well it control…
Matched conditions: CYSTINOSIS
Phase: PHASE1, PHASE2 • Sponsor: Nacuity Pharmaceuticals, Inc. • Aim: Disease control
Last updated May 26, 2026 05:54 UTC
-
Hope for cystinosis: drug may slow organ damage
Disease control Recruiting nowThis study follows 330 people with cystinosis, a rare inherited disease that causes kidney failure and growth problems. The drug cysteamine helps lower harmful cystine buildup in cells. Researchers aim to track long-term effects, spot new complications, and gather genetic data.
Matched conditions: CYSTINOSIS
Sponsor: National Human Genome Research Institute (NHGRI) • Aim: Disease control
Last updated May 22, 2026 13:53 UTC
-
New european study aims to unlock secrets of rare kidney disease
Knowledge-focused Recruiting nowThis study is gathering health information from 400 people with cystinosis, a rare genetic disease that causes cystine buildup and damages organs, especially the kidneys. By collecting data on symptoms, treatments, and quality of life, researchers hope to identify ways to improve…
Matched conditions: CYSTINOSIS
Sponsor: Institut National de la Santé Et de la Recherche Médicale, France • Aim: Knowledge-focused
Last updated May 22, 2026 14:04 UTC