Decades-Long study tracks rare disease treatment
NCT ID NCT00359684
Summary
This study monitors people with cystinosis, a rare inherited disease that causes kidney failure and organ damage, who are taking the medication cysteamine. Researchers will follow 330 patients over many years to track how well the treatment works and watch for any new complications. The goal is to better understand this rare disease and improve care for patients.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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National Institutes of Health Clinical Center
RECRUITINGBethesda, Maryland, 20892, United States
Conditions
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