Elpida Therapeutics Spc
Clinical trials sponsored by Elpida Therapeutics Spc, explained in plain language.
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Gene therapy breakthrough? new trial targets rare childhood paralysis
Disease control Recruiting nowThis study tests a one-time gene therapy called MELPIDA for children aged 4 months to 6 years with a rare genetic disease called SPG50, which causes progressive paralysis and developmental delays. The treatment is given as a single injection into the spinal fluid. The goal is to …
Phase: PHASE3 • Sponsor: Elpida Therapeutics SPC • Aim: Disease control
Last updated May 22, 2026 14:05 UTC
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Scientists watch rare nerve disease unfold in 20 patients
Knowledge-focused Recruiting nowThis study follows 20 people with a rare nerve disease called CMT4J for up to 2 years. Researchers will check participants once a year to see how the disease progresses. The goal is to learn more about the condition and find better ways to measure it in future studies.
Sponsor: Elpida Therapeutics SPC • Aim: Knowledge-focused
Last updated May 22, 2026 14:02 UTC