Elpida Therapeutics Spc
Clinical trials sponsored by Elpida Therapeutics Spc, explained in plain language.
-
One-Shot gene therapy offers hope for kids with rare, devastating movement disorder
Disease control Recruiting nowThis study is testing a one-time gene therapy injection for young children with a rare, inherited condition called SPG50 that severely affects movement and development. The therapy aims to deliver a working copy of the faulty gene directly to the nervous system to potentially slo…
Phase: PHASE3 • Sponsor: Elpida Therapeutics SPC • Aim: Disease control
Last updated Mar 20, 2026 14:48 UTC
-
Scientists track rare nerve disease to find better ways to measure it
Knowledge-focused Recruiting nowThis study aims to learn more about how a rare, inherited nerve disease called Charcot-Marie-Tooth type 4J (CMT4J) changes over time. It will follow 20 people of any age with a confirmed genetic diagnosis for up to two years, checking in annually with exams and tests. The goal is…
Sponsor: Elpida Therapeutics SPC • Aim: Knowledge-focused
Last updated Mar 25, 2026 14:08 UTC