Elpida Therapeutics Spc
Clinical trials sponsored by Elpida Therapeutics Spc, explained in plain language.
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Gene therapy hope for kids with rare paralysis: phase 3 trial launches
Disease control Recruiting nowThis study tests a one-time gene therapy called MELPIDA for children aged 4 months to 6 years with hereditary spastic paraplegia type 50 (SPG50), a rare genetic disease that causes progressive paralysis. The treatment is given as a single injection into the spinal fluid. The goal…
Phase: PHASE3 • Sponsor: Elpida Therapeutics SPC • Aim: Disease control
Last updated May 17, 2026 03:12 UTC
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New study tracks rare nerve disease to uncover its secrets
Knowledge-focused Recruiting nowThis study follows 20 people with a rare nerve disease called CMT4J to learn how the condition progresses. Participants of any age will be checked once a year for two years. The goal is to better understand the disease, not to test a treatment.
Sponsor: Elpida Therapeutics SPC • Aim: Knowledge-focused
Last updated May 07, 2026 18:39 UTC