Elpida Therapeutics Spc
Clinical trials sponsored by Elpida Therapeutics Spc, explained in plain language.
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Hope for kids with rare paralysis: gene therapy trial launches
Disease control Recruiting nowThis phase 3 trial tests a one-time gene therapy called MELPIDA for children with SPG50, a rare genetic disease that causes progressive paralysis and developmental delays. The study will give the treatment via a spinal injection to 24 children aged 4 months to 6 years and compare…
Phase: PHASE3 • Sponsor: Elpida Therapeutics SPC • Aim: Disease control
Last updated Jun 27, 2026 12:10 UTC
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Researchers track rare nerve disease to unlock future treatments
Knowledge-focused Recruiting nowThis study follows 20 people with a rare nerve disease called CMT4J for up to 2 years. Researchers will track symptoms and health changes to better understand how the disease progresses. The goal is to find better ways to measure the disease, which could help design future treatm…
Sponsor: Elpida Therapeutics SPC • Aim: Knowledge-focused
Last updated Jun 27, 2026 08:13 UTC