Askbio Inc
Clinical trials sponsored by Askbio Inc, explained in plain language.
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Gene therapy trial aims to ease Parkinson's symptoms
Disease control Recruiting nowThis study tests a gene therapy called AAV2-GDNF for people with moderate Parkinson's disease. The treatment is delivered directly to a brain area involved in movement. The goal is to see if it safely improves daily function. About 127 adults aged 45-75 with Parkinson's for 4-10 …
Phase: PHASE2 • Sponsor: AskBio Inc • Aim: Disease control
Last updated May 26, 2026 04:39 UTC
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Gene therapy shot could free pompe patients from weekly infusions
Disease control Recruiting nowThis early-stage trial is testing a single intravenous dose of a gene therapy called AB-1009 in 12 adults with late-onset Pompe disease. Participants must have been on standard enzyme replacement therapy for at least 6 months. The main goal is to check safety and see if the treat…
Phase: PHASE1, PHASE2 • Sponsor: AskBio Inc • Aim: Disease control
Last updated May 22, 2026 13:54 UTC
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Gene therapy trial opens for rare Muscle-Wasting condition
Disease control Recruiting nowThis study tests a single dose of a gene therapy called AB-1003 in 10 adults with limb girdle muscular dystrophy type 2I/R9, a genetic condition that weakens muscles. The main goal is to check safety and find the right dose. Participants must be able to walk 10 meters in under 30…
Phase: PHASE1, PHASE2 • Sponsor: AskBio Inc • Aim: Disease control
Last updated May 20, 2026 11:54 UTC