Askbio Inc
Clinical trials sponsored by Askbio Inc, explained in plain language.
-
First-in-Human gene therapy tested for rare muscle disease
Disease control OngoingThis is an early-stage safety study testing a new gene therapy called ACTUS-101 for adults with late-onset Pompe disease. The therapy aims to deliver a working copy of a missing gene to the liver to help the body produce a needed enzyme. The study will monitor seven participants …
Phase: PHASE1 • Sponsor: AskBio Inc • Aim: Disease control
Last updated Mar 27, 2026 12:38 UTC
-
Experimental gene therapy offers hope for failing hearts
Disease control OngoingThis study is testing whether a single dose of an experimental gene therapy called AB-1002 can help adults with advanced heart failure. About 150 participants with a specific type of heart failure will receive either the therapy or a placebo, delivered directly into their heart's…
Phase: PHASE2 • Sponsor: AskBio Inc • Aim: Disease control
Last updated Mar 19, 2026 14:56 UTC
-
Scientists track Long-Term effects of groundbreaking brain gene therapy
Knowledge-focused ENROLLING_BY_INVITATIONThis study is tracking the long-term safety and effectiveness of an experimental gene therapy called AB-1005 in people with Parkinson's disease or a related condition called MSA. It follows 132 participants who received the therapy in earlier trials to see how well they tolerate …
Sponsor: AskBio Inc • Aim: Knowledge-focused
Last updated Apr 02, 2026 14:57 UTC
-
Scientists closely monitor Parkinson's progression in landmark study
Knowledge-focused OngoingThis study aims to better understand how early Parkinson's disease and a related condition called multiple system atrophy progress over time. Researchers will follow 150 participants for 18 months, tracking their symptoms, movement abilities, and quality of life. The goal is to g…
Sponsor: AskBio Inc • Aim: Knowledge-focused
Last updated Apr 01, 2026 14:40 UTC