Mucopolysaccharidosis is

Clinical trials for Mucopolysaccharidosis is explained in plain language.

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Trials to join now! 1

First human trial launches for Gene-Based MPS i treatment

Disease control Recruiting now

This early-stage study tests whether ISP-001 is safe and tolerable in 11 people with a rare genetic disease called MPS I (Hurler-Scheie or Scheie types). Participants receive the experimental treatment and are monitored for side effects. The goal is to gather safety data for futu…

Matched conditions: MUCOPOLYSACCHARIDOSIS IS

Phase 1 • Sponsor: Immusoft of CA, Inc. • Aim: Disease control

Last updated Jul 19, 2026 00:00 UTC

Mucopolysaccharidosis is

Get alerted when new Mucopolysaccharidosis is trials appear

First human trial launches for Gene-Based MPS i treatment