MUCOPOLYSACCHARIDOSIS IS

Clinical trials for MUCOPOLYSACCHARIDOSIS IS explained in plain language.

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Trials to join now! 1

First-in-human trial aims to tame rare enzyme disorder

Disease control Recruiting now

This early-stage study tests a new therapy called ISP-001 in 11 people with MPS I (Hurler-Scheie or Scheie types). The main goal is to see if the treatment is safe and tolerable. Participants must be at least 10 years old and able to stay near the study site for a few days after …

Matched conditions: MUCOPOLYSACCHARIDOSIS IS

Phase: PHASE1 • Sponsor: Immusoft of CA, Inc. • Aim: Disease control

Last updated May 04, 2026 16:20 UTC

MUCOPOLYSACCHARIDOSIS IS

Get alerted when new MUCOPOLYSACCHARIDOSIS IS trials appear

First-in-human trial aims to tame rare enzyme disorder