HOMOZYGOUS FAMILIAL HYPERCHOLESTEROLEMIA
Clinical trials for HOMOZYGOUS FAMILIAL HYPERCHOLESTEROLEMIA explained in plain language.
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New hope for rare cholesterol disease: drug slashes dangerous LDL levels
Disease control CompletedThis study tested a new medicine called SHR-1918 in 55 people with homozygous familial hypercholesterolemia (HoFH), a rare genetic condition that causes extremely high cholesterol and early heart disease. Participants received either the drug or a placebo, and researchers measure…
Matched conditions: HOMOZYGOUS FAMILIAL HYPERCHOLESTEROLEMIA
Phase: PHASE3 • Sponsor: Beijing Suncadia Pharmaceuticals Co., Ltd • Aim: Disease control
Last updated May 26, 2026 12:12 UTC
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New registry tracks heart Drug's Long-Term safety in rare genetic disorder
Disease control CompletedThis study is a long-term registry that follows 260 patients with a rare genetic condition causing extremely high cholesterol (homozygous familial hypercholesterolemia) who are taking the drug lomitapide. The goal is to monitor safety over time, especially liver problems, stomach…
Matched conditions: HOMOZYGOUS FAMILIAL HYPERCHOLESTEROLEMIA
Sponsor: Amryt Pharma • Aim: Disease control
Last updated May 26, 2026 12:07 UTC
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New hope for rare cholesterol disease: drug shows promise in small trial
Disease control CompletedThis study tested a new medicine called SHR-1918 in 26 adults with homozygous familial hypercholesterolemia (HoFH), a rare genetic condition causing extremely high cholesterol. The goal was to see if the drug could safely lower their LDL (bad) cholesterol after 12 weeks. Particip…
Matched conditions: HOMOZYGOUS FAMILIAL HYPERCHOLESTEROLEMIA
Phase: PHASE2 • Sponsor: Beijing Suncadia Pharmaceuticals Co., Ltd • Aim: Disease control
Last updated May 22, 2026 13:50 UTC