HEMOPHILIA B
Clinical trials for HEMOPHILIA B explained in plain language.
Never miss a new study
Get alerted when new HEMOPHILIA B trials appear
Sign up with your email to follow new studies for HEMOPHILIA B, keep track of the ones that matter, and come back to a personal dashboard instead of checking manually.
Genom att skicka in godkänner du våra Användarvillkor
-
Gene therapy slashes bleeding in severe hemophilia b
Disease control CompletedThis study tested a single infusion of gene therapy (AMT-061) in 67 adults with severe or moderately severe hemophilia B. The treatment delivers a working copy of the factor IX gene to the liver, aiming to reduce bleeding episodes and the need for regular factor IX infusions. Res…
Matched conditions: HEMOPHILIA B
Phase: PHASE3 • Sponsor: CSL Behring • Aim: Disease control
Last updated May 26, 2026 09:27 UTC
-
Real-World data shows how alprolix controls bleeding in hemophilia b
Disease control CompletedThis study followed 151 people with hemophilia B for 24 months to see how well Alprolix works in everyday use. Researchers tracked bleeding episodes, how often the medicine was given, and how much was used. The goal was to understand real-world effectiveness, not to test a new tr…
Matched conditions: HEMOPHILIA B
Sponsor: Swedish Orphan Biovitrum • Aim: Disease control
Last updated May 19, 2026 11:59 UTC
-
Gene therapy trial offers hope for hemophilia b patients
Disease control CompletedThis early-stage study tested a new gene therapy for adults with severe hemophilia B, a bleeding disorder caused by a faulty gene. The treatment uses a harmless virus to deliver a working copy of the factor IX gene into the body. The main goal was to check safety in 14 participan…
Matched conditions: HEMOPHILIA B
Phase: PHASE1 • Sponsor: St. Jude Children's Research Hospital • Aim: Disease control
Last updated May 18, 2026 12:08 UTC
-
Hemophilia patients tracked before gene therapy push
Knowledge-focused CompletedThis study tracked 212 adults with moderately severe to severe hemophilia A or B for at least 6 months to record how often they bleed while on their usual clotting factor treatment. The information will be used as a baseline for future gene therapy studies. No experimental treatm…
Matched conditions: HEMOPHILIA B
Phase: PHASE3 • Sponsor: Pfizer • Aim: Knowledge-focused
Last updated May 22, 2026 14:02 UTC
-
Global survey reveals what hemophilia b patients really know about gene therapy
Knowledge-focused CompletedThis study interviewed 150 people with hemophilia B, their caregivers, and healthcare workers from around the world to find out what they know and think about gene therapy. The goal is to create better educational materials and improve the consent process, especially in countries…
Matched conditions: HEMOPHILIA B
Sponsor: St. Jude Children's Research Hospital • Aim: Knowledge-focused
Last updated May 18, 2026 12:11 UTC