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Thalassemia
MONDO:0000984An inherited blood disorder characterized by a decreased synthesis of one of the polypeptide chains that form hemoglobin. Anemia results from this abnormal hemoglobin formation.
Also known as: sickle-cell thalassemia with crisis, sickle-cell thalassemia without crisis
138 clinical trials for this condition and its sub-types, 49 tagged with Thalassemia itself.
Follow this condition to get notified about new trialsWhere it sits in the disease tree
Browse by category →Sub-types of Thalassemia
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Beta thalassemia 73 trials · 99 incl. sub-types
3 sub-types
- Beta-thalassemia HBB/LCRB 2 trials · 57 incl. sub-types Sub-types →
- Dominant beta-thalassemia 0 trials
- Thalassemia, beta+, silent allele 0 trials
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Alpha thalassemia spectrum 11 trials · 12 incl. sub-types
2 sub-types
- Digenic alpha thalassemia spectrum 0 trials · 8 incl. sub-types Sub-types →
- Monogenic alpha thalassemia spectrum 0 trials Sub-types →
Most studied deeper sub-types
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How does a blood disorder drug perform in everyday practice?
Knowledge-focused Stopped earlyThis study looks at how the drug luspatercept is used in real-world clinics for patients with lower-risk myelodysplastic syndromes (MDS) or beta-thalassemia. Researchers will track patient characteristics, treatments, and outcomes like reduced need for blood transfusions. The goa…
Sponsor: Bristol-Myers Squibb • Aim: Knowledge-focused
Last updated Jul 04, 2026 00:00 UTC
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New sickle cell drug pociredir enters early human testing
Knowledge-focused Stopped earlyThis early-stage study is testing a new drug called pociredir in 24 adults with sickle cell disease. Researchers want to see how the drug moves through the body and whether taking it with food changes its effects. The goal is to gather safety and dosing information, not to treat …
Phase 1 • Sponsor: Fulcrum Therapeutics • Aim: Knowledge-focused
Last updated Jun 27, 2026 14:00 UTC