Familial severe combined immunodeficiency
MONDO:003152024 clinical trials for this condition and its sub-types, 0 tagged with Familial severe combined immunodeficiency itself.
Follow this condition to get notified about new trialsWhere it sits in the disease tree
Browse by category →Sub-types of Familial severe combined immunodeficiency
-
Omenn syndrome 4 trials
-
MHC class II deficiency 1 trial
5 sub-types
- MHC class II deficiency 1 0 trials
- MHC class II deficiency 2 0 trials
- MHC class II deficiency 3 0 trials
- MHC class II deficiency 4 0 trials
- MHC class II deficiency 5 0 trials
-
Reticular dysgenesis 1 trial
1 sub-type
- Immunoerythromyeloid hypoplasia 0 trials
-
Cernunnos-XLF deficiency 0 trials
-
Immunodeficiency 104 0 trials
-
Immunodeficiency 105 0 trials
-
Immunodeficiency 18 0 trials
-
Immunodeficiency 19 0 trials
-
Immunodeficiency 49 0 trials
-
Bubble boy disease gene therapy trial launches
Disease control Not yet recruitingThis trial tests a gene therapy given by IV for X-linked severe combined immunodeficiency (SCID-X1), a rare immune disorder. Ten participants with no matched donor will receive a lentiviral vector to correct the genetic defect. The goal is to restore immune function and improve s…
Phase 1/2 • Sponsor: Shenzhen Geno-Immune Medical Institute • Aim: Disease control
Last updated Aug 29, 2026 00:00 UTC
-
One-Time gene fix could rescue 'Bubble Boy' disease
Disease control Not yet recruitingThis study tests a gene therapy given by IV for ADA-SCID, a rare and life-threatening immune disorder. The treatment uses a modified virus to deliver a working gene, aiming to restore the immune system. Ten participants will be monitored for safety and immune recovery over one ye…
Sponsor: Shenzhen Geno-Immune Medical Institute • Aim: Disease control
Last updated Aug 28, 2026 00:00 UTC