New hope for toddlers with rare bleeding disorder: wilate shows promise
NCT ID NCT04953884
First seen Jun 27, 2026 · Last updated Jun 27, 2026
Summary
This study tested a medicine called wilate in 12 children under 6 years old with severe von Willebrand disease, a bleeding disorder. The goal was to see if regular infusions of wilate could prevent bleeding episodes over 12 months. Researchers measured how many bleeds occurred, how the drug moved through the body, and any side effects. The treatment aims to control the disease, not cure it.
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the original study
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Conditions
The condition(s) this trial relates to.
As listed by the trial registrant
The condition terms exactly as the trial's registrant entered them.
Contacts and locations
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Locations
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Danylo Halytsky Lviv National Medical University, Communal Institution of Lviv Regional Council "Western Ukrainian Specialized Children's Medical Centre"
Lviv, Ukraine
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FSBI National Research Medical Center of Pediatric Hematology, Oncology and Immunology
Moscow, Russia
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Gerinnungszentrum Rhein-Ruhr Ambulanz und Fachlaboratorium für Gerinnungserkrankungen/Hämophilie
Duisburg, Germany
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IMSP Mother and Child Institute
Chisinau, Moldova
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Morozovskaya Children's Hospital
Moscow, Russia
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PHI University Clinic for Child Diseases
Skopje, North Macedonia
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Tulane University
New Orleans, Louisiana, 70118, United States
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University Hospital Motol, Department of Paediatric Haematology and Oncology
Prague, Czechia
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University Hospital Ostrava Department for Pediatric Medicine
Ostrava, Czechia