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New hope for kids with rare bleeding disorder: drug aims to stop bleeds before they start

NCT ID NCT05582993

Recruiting now Disease control Sponsor: Takeda Source: ClinicalTrials.gov ↗

First seen Jun 27, 2026 · Last updated Jun 27, 2026

Summary

This study tests a drug called vonicog alfa to prevent bleeding in 24 children with severe von Willebrand disease, a condition that causes easy bruising and heavy bleeding. Participants receive the drug regularly for 12 months to see if it reduces bleeding episodes compared to their past experiences. The goal is to improve daily life by controlling the disease with ongoing treatment.

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Conditions

The condition(s) this trial relates to.

hereditary von Willebrand disease von Willebrand disease (hereditary or acquired)

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

VON WILLEBRAND DISEASE (VWD)

Contacts and locations

Study contacts

  • Contact

    Email: •••••@•••••

Locations

  • Azienda Ospedaliera Pediatrica Santobono Pausillipon

    ACTIVE_NOT_RECRUITING

    Naples, 80123, Italy

  • Azienda Ospedaliero-Universitaria Città della Salute e della Scienza di Torino

    ACTIVE_NOT_RECRUITING

    Turin (Torino), 10126, Italy

  • Bleeding and Clotting Disorders Institute

    RECRUITING

    Peoria, Illinois, 61614, United States

  • Children's Health Care d/b/a Children's Minnesota

    RECRUITING

    Minneapolis, Minnesota, 55404, United States

  • Children's Health Ireland

    RECRUITING

    Dublin, D12N512, Ireland

  • Childrens Hospital of Michigan

    RECRUITING

    Detroit, Michigan, 48201, United States

  • Cure 4 the Kids

    RECRUITING

    Las Vegas, Nevada, 89135, United States

  • Haemophilia Comprehensive Care Centre, Great Ormond Street Hospital for Children NHS Foundation Trust

    RECRUITING

    London, WC1N 3HR, United Kingdom

  • Hemostase Clinique - Institut Cœur-Poumons (4eme étage aile est) Bureau 419

    RECRUITING

    Lille, 59037, France

  • Hopital Edouard Herriot - CHU Lyon

    RECRUITING

    Lyon, 69677, France

  • Japanese Red Cross Narita Hospital

    RECRUITING

    Narita, Chiba, 286-8523, Japan

  • Medical University of South Carolina (MUSC)

    RECRUITING

    Charleston, South Carolina, 29425, United States

  • Michigan State University Center for Bleeding Disorders & Clotting Disorders

    RECRUITING

    East Lansing, Michigan, 48824, United States

  • NHO Beppu Medical Center

    RECRUITING

    Beppu, Oita Prefecture, 874-0011, Japan

  • Nagasaki University Hospital

    RECRUITING

    Nagasaki, 852-8501, Japan

  • Nara Medical University Hospital

    RECRUITING

    Kashihara, Nara, 634-8522, Japan

  • New York - Presbyterian/Weill Cornell Medical Center

    RECRUITING

    New York, New York, 10021, United States

  • Riley Hospital for Children Indiana University Health

    RECRUITING

    Indianapolis, Indiana, 46202, United States

  • Rutgers - Robert Wood Johnson Medical School

    RECRUITING

    New Brunswick, New Jersey, 08901, United States

  • University of Alabama at Birmingham

    RECRUITING

    Birmingham, Alabama, 35223, United States

  • University of Iowa Hospitals & Clinics PARENT

    RECRUITING

    Iowa City, Iowa, 52242, United States

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