New hope for rare bone cancer? drug shows promise in early trial

NCT ID NCT01267955

First seen Jun 27, 2026 · Last updated Jun 27, 2026

Summary

This phase 2 trial tested vismodegib, a pill that targets a specific growth pathway, in 45 people with advanced chondrosarcoma (a rare bone cancer). The goal was to see if the drug could shrink tumors or stop them from growing. Participants had to have measurable disease and no more than three prior chemotherapy treatments. The study used a two-stage design to decide if the drug was worth further study.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

Vismodegib (a targeted cancer drug taken by mouth)

What this could lead to

If it works, this could provide a new treatment option for people with advanced chondrosarcoma, a rare bone cancer that currently has few effective therapies.

What could go wrong

This is a small, early-phase trial with only 45 participants, so results may not apply to everyone. The drug may not shrink tumors or improve survival, and side effects like muscle spasms, hair loss, and fatigue are common.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

chondrosarcoma Chondrosarcoma, Clear Cell clear cell chondrosarcoma dedifferentiated chondrosarcoma mesenchymal chondrosarcoma

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Centre Leon Berard

    Lyon, 69373, France

  • Centre Oscar Lambert

    Lille, 59020, France

  • Gustave Roussy

    Villejuif, 94805, France

  • Hopital De La Timone

    Marseille, 13385, France

  • Institut Bergonie Cancer Center

    Bordeaux, 33076, France

  • Institut Curie Paris

    Paris, 75005, France