Last-resort leukemia combo shows early promise in tiny trial

NCT ID NCT04926285

First seen Jun 27, 2026 · Last updated Jun 27, 2026

Summary

This early-phase study tested a combination of two drugs, venetoclax and omacetaxine, in 6 adults with acute myeloid leukemia (AML) whose cancer had stopped responding to venetoclax-based treatments. The main goal was to find the safest dose of omacetaxine when given with venetoclax. Researchers also looked for signs that the cancer shrank or disappeared. Because the trial is very small and early, it cannot yet say whether this combination works well.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

Venetoclax and omacetaxine

What this could lead to

If this works, it could offer a new treatment option for people with acute myeloid leukemia whose cancer has stopped responding to venetoclax.

What could go wrong

This is a very early, small study (only 6 people) to find the right dose and check safety. It is not yet designed to prove the combination works, and side effects are unknown.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

acute myeloid leukemia hematopoietic and lymphoid system neoplasm Recurrence refractory hematologic cancer

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • University of Illinois Cancer Center

    Chicago, Illinois, 60612, United States