New drug tofersen under safety watch for rare ALS in china

NCT ID NCT07223723

First seen Nov 03, 2025 · Last updated May 13, 2026 · Updated 27 times

Summary

This study checks the long-term safety of tofersen (Qalsody) in 12 Chinese adults with a specific genetic type of ALS (SOD1-ALS). Participants receive 13 doses injected into the spine over a year. The main goal is to track side effects and how the drug moves through the body.

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Contacts and locations

Study contacts

  • Contact

    Email: •••••@•••••

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Peking University Third Hospital

    RECRUITING

    Beijing, Beijing Municipality, 100083, China

Conditions

Explore the condition pages connected to this study.