Scientists test approved ALS drug on wider patient group

NCT ID NCT07294144

Summary

This study is testing whether tofersen, a drug already approved for a specific genetic form of ALS, is safe and can lower a key disease marker in people with ALS who do not have that specific gene mutation. About 30 adults with early-stage ALS will receive the drug via spinal injections over 24 weeks. Researchers will measure a protein in the blood and spinal fluid linked to nerve damage, monitor safety, and track symptoms and quality of life.

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Contacts and locations

Locations

  • Washington University ALS Center

    RECRUITING

    St Louis, Missouri, 63110, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

Conditions

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